Tividenofusp Alfa Treatment in a Male Sibling Pair with Non-Neuronopathic Mucopolysaccharidosis Type II
Irene J Chang,1 Jacqueline Madden,1 Annie Sako,1 Jill Dwyer,1 Daniel Fertek,2 Adam Scheller,2 Sharon O’Byrne,2 Imanol Zubizarreta Arambarri,2 Peter Chin,2 Paul Harmatz1
1 UCSF Benioff Children’s Hospital, Oakland, CA, USA; 2 Denali Therapeutics Inc., South San Francisco, CA, USA
Supplementary Videos
Both siblings at approximately Week 153
Week 165
Week 124
Both siblings have received treatment with tividenofusp alfa for at least 124 weeks.
Supplementary Images
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